Study design & results
Available in the Gosset platform where reported.
Trial intelligence / Profile preview
NCT04863794Phase 1Completed
Phase 1, open-label, single-arm trial of rugonersen in Angelman syndrome (AS), sponsored by Roche. Primary endpoint: Quantification of [89Zr]DFO-RO7248824 distribution within the central nervous system (CNS). Started Apr 2021; status: completed.
Beyond the preview
Study design, results and competitive context are available in the Gosset platform where reported.
Available in the Gosset platform where reported.
Available in the Gosset platform where reported.
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