Trial intelligence / Profile preview

PK, Safety, and Efficacy of Vatiquinone in Children < 7 Years with Friedreich Ataxia

NCT05485987Phase 2Completed

Sponsor
PTC Therapeutics, Inc.
Start
Oct 2022
Primary completion
Aug 2024
Modality
Small Molecules
Countries
1
01

Overview

A Phase 2 trial of vatiquinone in Friedreich ataxia (FA), sponsored by PTC Therapeutics, Inc.. Started Oct 2022; status: completed.

02

Drugs

vatiquinone
03

Conditions

Friedreich ataxia (FA)

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