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RAINBOW: AZ-3102 in GM2 Gangliosidosis or Niemann-Pick Type C Disease
NCT05758922Phase 2Completed
- Sponsor
- Azafaros
- Start
- Apr 2023
- Primary completion
- Apr 2024
- Modality
- Orthosteric Ligands
- Countries
- 1
01
Overview
A Phase 2 trial of nizubaglustat in GM2 gangliosidosis, Niemann-Pick disease type C (NPC), sponsored by Azafaros. Started Apr 2023; status: completed.
02
Drugs
nizubaglustat
03
Conditions
GM2 gangliosidosisNiemann-Pick disease type C (NPC)
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