Trial intelligence / Profile preview

HGI-001 in Transfusion-Dependent β-Thalassemia

NCT05864170Phase 1Recruiting

Sponsor
Shenzhen Hemogen Therapeutic Co., Ltd.
Start
May 2022
Primary completion
Dec 2025
Modality
Gene Editing, Gene Silencing, Cell Therapies
Countries
1
01

Overview

Phase 1, open-label, single-arm trial of LentiHBBT87Q in beta thalassemia, sponsored by Shenzhen Hemogen Therapeutic Co., Ltd. Primary endpoints: Overall response rate at 24 months, Incidence and severity of AEs at 24 months and 6 more. Started May 2022; status: recruiting.

02

Drugs

LentiHBBT87Q
03

Conditions

beta thalassemia

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