Trial intelligence / Profile preview

ER2001 in early manifest Huntington's disease

NCT06024265Phase 1Completed

Sponsor
ExoRNA Bioscience
Start
Apr 2023
Primary completion
Jan 2025
Modality
Gene Editing, Gene Silencing, Lipid-based Nanoparticles
Countries
1
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Overview

Phase 1, open-label, single-arm trial of ER2001 in Huntington's disease (HD), sponsored by ExoRNA Bioscience. Primary endpoint: Incidence and Severity of Adverse Events and Serious Adverse Events at 6.5 months. Started Apr 2023; status: completed.

02

Drugs

ER2001
03

Conditions

Huntington's disease (HD)

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