Trial intelligence / Profile preview

VGN-R08b in Type II Gaucher Disease

NCT06272149Phase 1Recruiting

Sponsor
Xinhua Hospital
Start
Mar 2023
Primary completion
Jan 2025
Modality
Gene Editing, Gene Silencing, Small Molecules
Countries
1
01

Overview

Phase 1, open-label, single-arm trial of VGN-R08b in Gaucher disease type 2 (GD2), sponsored by Xinhua Hospital. Primary endpoint: Number of Adverse Events (AEs), Serious Adverse Events (SAEs) at 52 weeks. Started Mar 2023; status: recruiting.

02

Drugs

VGN-R08b
03

Conditions

Gaucher disease type 2 (GD2)

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