Trial intelligence / Profile preview

GTX-102 Long-term Extension in Angelman Syndrome

NCT06415344Phase 3Terminated

Sponsor
Ultragenyx Pharmaceutical Inc.
Start
Jul 2024
Primary completion
Oct 2026
Modality
Modified DNA Oligonucleotides, Single-strand DNA, Antisense Oligonucleotides (ASOs)
Countries
8
01

Overview

A Phase 3 trial of apazunersen in Angelman syndrome (AS), sponsored by Ultragenyx Pharmaceutical Inc.. Started Jul 2024; status: terminated.

02

Drugs

apazunersen
03

Conditions

Angelman syndrome (AS)

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