Trial intelligence / Profile preview

RJK002 in amyotrophic lateral sclerosis

NCT06493279Phase 1Active, not recruiting

Sponsor
RJK Biopharma
Start
Sep 2024
Primary completion
Nov 2026
Modality
Gene Editing, Gene Silencing, Gene Addition/Replacement
Countries
1
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Overview

Phase 1, open-label, single-arm trial of RJK002 in amyotrophic lateral sclerosis (ALS), sponsored by RJK Biopharma. Primary endpoints: Adverse Events/Serious Adverse Events at 5 years and Dose Limiting Toxicities at 28 days. Started Sep 2024; status: active, not recruiting.

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Drugs

RJK002
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Conditions

amyotrophic lateral sclerosis (ALS)

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