Trial intelligence / Profile preview

GTX-102 in Angelman Syndrome

NCT07157254Phase 2Terminated

Sponsor
Ultragenyx Pharmaceutical Inc.
Start
Oct 2025
Primary completion
Oct 2026
Modality
Modified DNA Oligonucleotides, Single-strand DNA, Antisense Oligonucleotides (ASOs)
Countries
8
01

Overview

A Phase 2 trial of apazunersen in Angelman syndrome (AS), sponsored by Ultragenyx Pharmaceutical Inc.. Started Oct 2025; status: terminated.

02

Drugs

apazunersen
03

Conditions

Angelman syndrome (AS)

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