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nL-TUBB4-001 for TUBB4A-related leukodystrophy
NCT07222371Phase 2Active, not recruiting
- Sponsor
- University of California, San Diego
- Start
- Sep 2025
- Primary completion
- Sep 2027
- Modality
- Modified DNA Oligonucleotides, Single-strand DNA, Antisense Oligonucleotides (ASOs)
- Countries
- 1
01
Overview
A Phase 2 trial of nL-TUBB4-001 in TUBB4A-related leukodystrophy, sponsored by University of California, San Diego. Started Sep 2025; status: active, not recruiting.
02
Drugs
nL-TUBB4-001
03
Conditions
TUBB4A-related leukodystrophy
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