Trial intelligence / Profile preview

Individualized ASOs in Pediatric SDLT CNS Disorders

NCT07410143Phase 2Active, not recruiting

Sponsor
EveryONE Medicines
Start
Jan 2026
Primary completion
Sep 2026
Modality
Modified DNA Oligonucleotides, Single-strand DNA, Antisense Oligonucleotides (ASOs)
Countries
1
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Overview

Phase 2, open-label, single-arm trial of individualized antisense oligonucleotide in central nervous system disorder (CNSD), sponsored by EveryONE Medicines. Primary endpoint: Incidence of Treatment-Emergent Adverse Events at 48 weeks. Started Jan 2026; status: active, not recruiting.

02

Drugs

individualized antisense oligonucleotide
03

Conditions

central nervous system disorder (CNSD)

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