Trial intelligence / Profile preview

Phase 1 Study of CTX001 in Healthy Adults

NCT07577817Phase 1Recruiting

Sponsor
Cajal Therapeutics
Start
Jun 2026
Primary completion
Oct 2026
Modality
Gene Silencing, CRISPR-Cas9, Cell Therapies
Countries
1
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Overview

Phase 1, randomised, double-blind trial of exagamglogene autotemcel in anemia, iron deficiency anemia (IDA) and chronic kidney disease (CKD) (6 arms), sponsored by Cajal Therapeutics. Primary endpoints: Treatment-Emergent Adverse Events at 15 days, Serious Treatment-Emergent Adverse Events at 15 days and 4 more. Started Jun 2026; status: recruiting.

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Drugs

exagamglogene autotemcel
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Conditions

anemiairon deficiency anemia (IDA)chronic kidney disease (CKD)

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