Trial intelligence / Profile preview

VSA012 in Complement Inhibitor-Naive Paroxysmal Nocturnal Hemoglobinuria

NCT07816237Phase 3Not yet recruiting

Sponsor
BiSiRNA Therapeutics
Start
Oct 2026
Primary completion
Sep 2027
Countries
1
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Overview

Phase 3, randomised, open-label trial of VSA012 in paroxysmal nocturnal hemoglobinuria (PNH) (2 arms), sponsored by BiSiRNA Therapeutics. Primary endpoint: Proportion of patients with sustained hemoglobin levels >= 120 g/L without RBC transfusion. Planned start Oct 2026; status: not yet recruiting.

02

Drugs

VSA012
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Conditions

paroxysmal nocturnal hemoglobinuria (PNH)

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