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Long-term follow-up of Myozyme treatment in children and adults with Pompe disease
NL-OMON47930Recruiting
- Sponsor
- Erasmus MC
- Start
- Jun 2007
- Modality
- Replacement Enzymes → Therapeutic Enzymes → Recombinant Proteins and Enzymes
- Countries
- 1
01
Overview
Open-label trial of alglucosidase alfa in Pompe disease (3 arms), sponsored by Erasmus MC. Primary endpoints: Survival, Muscle strength and function and 21 more. Started Jun 2007; status: recruiting.
02
Drugs
alglucosidase alfa
03
Conditions
Pompe disease
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