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Pediatric eliglustat study in Gaucher disease type 1 and type 3
NL-OMON48873Phase 3Withdrawn
- Sponsor
- Sanofi
- Start
- Jun 2018
- Modality
- Small Molecules, Replacement Enzymes → Therapeutic Enzymes → Recombinant Proteins and Enzymes
- Countries
- 1
01
Overview
Phase 3, open-label trial of eliglustat and imiglucerase in Gaucher disease type 1 (GD1) and Gaucher disease type 3 (2 cohorts), sponsored by Sanofi. Primary endpoints: Safety of eliglustat in pediatric patients and Pharmacokinetics of eliglustat in pediatric patients. Planned start Jun 2018; status: withdrawn.
02
Drugs
eliglustatimiglucerase
03
Conditions
Gaucher disease type 1 (GD1)Gaucher disease type 3
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