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Long-term follow-up study of RGX-501 in homozygous familial hypercholesterolemia
NL-OMON49424Phase 2Completed
- Sponsor
- REGENXBIO Inc.
- Start
- Nov 2020
- Modality
- Gene Therapies
- Countries
- 1
01
Overview
Phase 2, open-label, single-arm trial of AAV-hLDLR in familial hypercholesterolemia (FH), sponsored by REGENXBIO Inc. Primary endpoint: Long-term safety of RGX-501. Started Nov 2020; status: completed.
02
Drugs
AAV-hLDLR
03
Conditions
familial hypercholesterolemia (FH)
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