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Long-term follow-up of eli-cel-treated subjects with cerebral adrenoleukodystrophy
NL-OMON54368Phase 3Recruiting
- Sponsor
- bluebird bio, Inc.
- Start
- Feb 2022
- Modality
- Cell Therapies, Gene Therapies
- Countries
- 1
01
Overview
Phase 3, open-label, single-arm trial of elivaldogene autotemcel in cerebral adrenoleukodystrophy (CALD), sponsored by bluebird bio, Inc. Primary endpoints: Proportion of subjects who experience graft versus host disease, Proportion of subjects who undergo subsequent stem cell transplantation and 7 more. Started Feb 2022; status: recruiting.
02
Drugs
elivaldogene autotemcel
03
Conditions
cerebral adrenoleukodystrophy (CALD)
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