Trial intelligence / Profile preview

Phase 3 study of AOC 1001 in myotonic dystrophy type 1

NL-OMON58999Phase 3Completed

Sponsor
Avidity Biosciences
Start
Dec 2024
Modality
Antibody Conjugates → Antibody-Based Therapeutics, Chemically Modified siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Conjugated siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
Countries
1
01

Overview

Phase 3 trial of delpacibart etedesiran in myotonic dystrophy type 1 (DM1), sponsored by Avidity Biosciences. Primary endpoint: Change from baseline to Week 54 in video Hand Opening Time. Started Dec 2024; status: completed.

02

Drugs

delpacibart etedesiran
03

Conditions

myotonic dystrophy type 1 (DM1)

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