Trial intelligence / Profile preview

SYNAPSE-SMA trial of NMD670 in ambulatory adults with type 3 spinal muscular atrophy

NL-OMON59138Phase 2Completed

Sponsor
NMD Pharma
Start
Sep 2023
Modality
Small Molecules
Countries
1
01

Overview

Phase 2, randomised, double-blind trial in Spinal muscular atrophy type 3 (SMA3) comparing NMD670 with Placebo (2 arms). Primary endpoint: Change from baseline in 6-minute walk test total distance after 21-day dosing. Started Sep 2023; status: completed.

02

Drugs

ignaseclant
03

Conditions

Spinal muscular atrophy type 3 (SMA3)

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