Trial intelligence / Profile preview

Enzyme replacement therapy in children and adults with Pompe disease

NL-OMON60102Phase 4Not yet recruiting

Sponsor
Erasmus MC
Start
Jun 2007
Modality
Replacement Enzymes → Therapeutic Enzymes → Recombinant Proteins and Enzymes
Countries
1
01

Overview

Phase 4, open-label, single-arm trial of alglucosidase alfa in Pompe disease, sponsored by Erasmus MC. Primary endpoints: Survival, Muscle strength and function and 7 more. Planned start Jun 2007; status: not yet recruiting.

02

Drugs

alglucosidase alfa
03

Conditions

Pompe disease

Beyond the preview

Go deeper on NL-OMON60102.

Study design, results and competitive context are available in the Gosset platform where reported.

Study design & results

Available in the Gosset platform where reported.

Competitive context

Available in the Gosset platform where reported.

Bring the full picture into focus.

See how Gosset can support your research on NL-OMON60102.

Gosset Free

Get started with Gosset.

Enter your corporate email.

Work email preferred.

Book a call