Trial intelligence / Profile preview

Phase 1 safety, tolerability, PK and PD study of AX-0810 in healthy participants

NL-OMON60967Phase 1Completed

Sponsor
ProQR Therapeutics
Start
Nov 2025
Modality
Gene Editing → Gene Therapies, Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, MicroRNA (miRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
Countries
1
01

Overview

Phase 1, single-arm trial of PR1100 in cholestatic disease, sponsored by ProQR Therapeutics. Primary endpoint: Primary endpoint(s). Started Nov 2025; status: completed.

02

Drugs

PR1100
03

Conditions

cholestatic disease

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