Trial intelligence / Profile preview

ONCE: Once-daily eliglustat in stable CYP2D6 intermediate and extensive metabolizers with Gaucher disease type 1

NL-OMON61759Phase 4Not yet recruiting

Sponsor
Amsterdam University Medical Center
Start
Oct 2026
Modality
Small Molecules
Countries
1
01

Overview

Phase 4, open-label, single-arm trial of eliglustat in Gaucher disease type 1 (GD1), sponsored by Amsterdam University Medical Center. Primary endpoint: Clinical stability at Month 12. Planned start Oct 2026; status: not yet recruiting.

02

Drugs

eliglustat
03

Conditions

Gaucher disease type 1 (GD1)

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