Trial intelligence / Profile preview

Etavopivat in children with sickle cell disease

PACTR202603858736405Phase 3Not yet recruiting

Sponsor
Novo Nordisk
Start
Nov 2026
Modality
Small Molecules
Countries
2
01

Overview

Phase 3, randomised, double-blind trial in sickle cell disease (SCD) comparing Etavopivat with Placebo (2 arms). Primary endpoint: Annualised rate of adjudicated vaso-occlusive crisis events with a medical contact. Planned start Nov 2026; status: not yet recruiting.

02

Drugs

etavopivat
03

Conditions

sickle cell disease (SCD)

Beyond the preview

Go deeper on PACTR202603858736405.

Study design, results and competitive context are available in the Gosset platform where reported.

Study design & results

Available in the Gosset platform where reported.

Competitive context

Available in the Gosset platform where reported.

Bring the full picture into focus.

See how Gosset can support your research on PACTR202603858736405.

Gosset Free

Get started with Gosset.

Enter your corporate email.

Work email preferred.

Book a call